A diagram showing a triangle connecting three Duchenne muscular dystrophy (DMD) models: a zebrafish (top), a rat (bottom left), and fluorescent-stained human induced pluripotent stem cells (hiPSCs, bottom right).

NIH Funds Collaborative Effort to Pinpoint the Origins of Duchenne Muscular Dystrophy

February 18, 2021 | Categories: Award, Core Faculty, Research | Tagged: , , , , , ,

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Three microscopic images of mouse heart muscle tissue, labeled a, b, and c, with text describing the results of micro-dystrophin gene therapy for Duchenne muscular dystrophy. Images show green-stained muscle fibers with varying patterns.

Gene Therapy Cassettes Improved for Muscular Dystrophy

February 1, 2019 | Categories: Research | Tagged: , , ,

February 1, 2019 Experimental gene therapy cassettes for Duchenne muscular dystrophy have been modified to deliver better performance.  The cassettes, which carry the therapy into muscle cells, contain newer versions […] Read More