Two men wearing white lab coats stand and smile in a laboratory. Shelves with lab equipment and supplies are visible in the background, and a window lets in natural light.

New Gene Therapy for Muscular Dystrophy Offers Hope

July 17, 2024 | Categories: Core Faculty, Research | Tagged: , ,

A new gene therapy treatment for Duchenne muscular dystrophy (DMD) shows promise of not only arresting the decline of the muscles of those affected by this inherited genetic disease, but perhaps, in the future, repairing those muscles. Read More

Side-by-side photos of two men: the left man with short light brown hair wearing a light purple shirt, and the right man with short dark curly hair wearing a dark polo shirt, smiling in a room with shelves behind him.

Meet the 2024 Tietze Award Winners

May 24, 2024 | Categories: Award, Core Faculty | Tagged: , ,

ISCRM Associate Director Nate Sniadecki, PhD, Professor of Mechanical Engineering and Hichem Tasfaout, PhD, Acting Assistant Professor, Neurology have received prestigious awards from the John H. Tietze Foundation Trust that will help fuel promising research underway in their labs. Read More

A smiling man with short brown hair and glasses, wearing a dark shirt and lanyard, stands indoors in front of a window with green foliage visible outside.

FDA Approves Gene Therapy with ISCRM Origins

July 5, 2023 | Categories: Core Faculty, Research | Tagged: , , ,

The FDA has approved a first-ever gene therapy for Duchenne muscular dystrophy based in part on technology developed by UW Medicine/ISCRM Researchers Read More

A diagram showing a triangle connecting three Duchenne muscular dystrophy (DMD) models: a zebrafish (top), a rat (bottom left), and fluorescent-stained human induced pluripotent stem cells (hiPSCs, bottom right).

NIH Funds Collaborative Effort to Pinpoint the Origins of Duchenne Muscular Dystrophy

February 18, 2021 | Categories: Award, Core Faculty, Research | Tagged: , , , , , ,

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Three microscopic images of mouse heart muscle tissue, labeled a, b, and c, with text describing the results of micro-dystrophin gene therapy for Duchenne muscular dystrophy. Images show green-stained muscle fibers with varying patterns.

Gene Therapy Cassettes Improved for Muscular Dystrophy

February 1, 2019 | Categories: Research | Tagged: , , ,

February 1, 2019 Experimental gene therapy cassettes for Duchenne muscular dystrophy have been modified to deliver better performance.  The cassettes, which carry the therapy into muscle cells, contain newer versions […] Read More