New Gene Therapy for Muscular Dystrophy Offers Hope
July 17, 2024 | Categories: Core Faculty, Research |A new gene therapy treatment for Duchenne muscular dystrophy (DMD) shows promise of not only arresting the decline of the muscles of those affected by this inherited genetic disease, but perhaps, in the future, repairing those muscles. Read More
New Insights from Mack Lab on Mechanisms of Gene Therapy for X-Linked Myotubular Myopathy
January 27, 2020 | Categories: Research |
Gene Therapy Cassettes Improved for Muscular Dystrophy
February 1, 2019 | Categories: Research |February 1, 2019 Experimental gene therapy cassettes for Duchenne muscular dystrophy have been modified to deliver better performance. The cassettes, which carry the therapy into muscle cells, contain newer versions […] Read More
Favorable interim results reported in stem-cell therapy trial
January 8, 2018 | Categories: Research |A therapy developed at UW shows promise in its first test in young boys who have an inherited deadly muscle disease. Favorable interim results have been announced in a small clinical trial of a stem-cell therapy to treat patients with a rare, deadly disease called myotubular myopathy. Read More
Gene therapy treats muscle-wasting disease in dogs
February 15, 2017 | Categories: Research |Work on gene therapy is showing significant progress for restoring muscle strength and prolonging lives in dogs with a previously incurable, inherited neuromuscular disease. UW Medicine Institute for Stem Cell […] Read More
New book published on regenerative medicine for degenerative muscle diseases
January 12, 2016 | Categories: Announcements |Congratulations to ISCRM’s Casey Childers and Hannele Ruohola-Baker who are contributing authors of a new book entitled Regenerative Medicine for Muscle Diseases. The book, edited by Casey Childers, delves into […] Read More
ISCRM Faculty Member featured in The Scientist
December 1, 2015 | Categories: Announcements |The work of ISCRM faculty member, Casey Childers, on a gene therapy in children with a rare and fatal muscle weakness disorder called X-linked myotubular myopathy was highlighted in a Dec. 1, […] Read More