New Insights from Mack Lab on Mechanisms of Gene Therapy for X-Linked Myotubular Myopathy
January 27, 2020 | Categories: Research |
Favorable interim results reported in stem-cell therapy trial
January 8, 2018 | Categories: Research |A therapy developed at UW shows promise in its first test in young boys who have an inherited deadly muscle disease. Favorable interim results have been announced in a small clinical trial of a stem-cell therapy to treat patients with a rare, deadly disease called myotubular myopathy. Read More
Gene replacement therapy that works in dogs to be tested in children
May 18, 2017 | Categories: Research |SEATTLE – KIRO 7 has learned of a revolutionary treatment, here in Seattle, that has saved the lives of dogs and is just months away from being tested in children. In […] Read More
UW, family rewriting neuromuscular research
November 23, 2016 | Categories: Announcements |Physicians and researchers at the UW Medicine Institute for Stem Cell and Regenerative Medicine have partnered up with a nonprofit foundation in one of the leading efforts to find a cure […] Read More
Gene therapy leads to robust improvements in animal model of fatal muscle disease
January 22, 2014 | Categories: Research |January 22, 2014 Preclinical studies show that gene therapy can improve muscle strength in small- and large-animal models of a fatal congenital childhood disease know as X-linked myotubular myopathy. The […] Read More